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GeneTx and Ultragenyx Announce Positive Interim Phase 1/2 Data

GeneTx and Ultragenyx Announce Positive Interim Phase 1/2 Data

admin Oct 27,2020

“So far we are seeing rapid improvements in multiple areas, including some kids doing things they’ve never done before, and I don’t believe this rate of progress in development skills has been seen before in Angelman syndrome,” commented Elizabeth M. Berry-Kravis, M.D. investigator in the GTX-102 clinical study.

Roche Clinical trial

Roche Clinical trial

Jun 23,2020

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Global Angelman Syndrome Registry collaboration

Global Angelman Syndrome Registry collaboration

Dec 20,2019

We are proud to collaborate with the Angelman Syndrome Foundation, the Dup15q Alliance in Linking Angelman and Dup15q Data for Expanded Research (LADDER).