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GeneTx and Ultragenyx Announce Positive Interim Phase 1/2 Data
admin Oct 27,2020“So far we are seeing rapid improvements in multiple areas, including some kids doing things they’ve never done before, and I don’t believe this rate of progress in development skills has been seen before in Angelman syndrome,” commented Elizabeth M. Berry-Kravis, M.D. investigator in the GTX-102 clinical study.
Angelman syndrome biobank
Oct 06,2020Roche Clinical trial
Jun 23,2020Other News
Global Angelman Syndrome Registry collaboration
Dec 20,2019We are proud to collaborate with the Angelman Syndrome Foundation, the Dup15q Alliance in Linking Angelman and Dup15q Data for Expanded Research (LADDER).